A Preclinical Study Evaluating AAVrh10-Based Gene Therapy for Sanfilippo Syndrome

2016 ◽  
Vol 27 (5) ◽  
pp. 363-375 ◽  
Author(s):  
Leanne K. Winner ◽  
Helen Beard ◽  
Sofia Hassiotis ◽  
Adeline A. Lau ◽  
Amanda J. Luck ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Preclinical Study ◽  
Sanfilippo Syndrome

Long-term hematopoietic stem cell gene therapy corrects neuromuscular manifestations in preclinical study of Pompe mice

2021 ◽  
Vol 132 (2) ◽  
pp. S107
Author(s):  
Niek P. van Til ◽  
Yildirim Dogan ◽  
Cecilia Barese ◽  
Zeenath Unnisa ◽  
Swaroopa Guda ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Hematopoietic Stem Cell ◽  
Preclinical Study ◽  
Hematopoietic Stem ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy

Abstract A17: Challenging pancreatic ductal adenocarcinoma and its stroma by a combination of chemo and gene therapy: A preclinical study

2019 ◽  
Author(s):  
Giulia Grisendi ◽  
Massimiliano Dall'Ora ◽  
Angela D'Esposito ◽  
Giulia Casaria ◽  
Carlotta Spano ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Pancreatic Ductal Adenocarcinoma ◽  
Preclinical Study ◽  
Ductal Adenocarcinoma

scholarly journals Preclinical study on combined chemo- and nonviral gene therapy for sensitization of melanoma using a human TNF-alpha expressing MIDGE DNA vector

2014 ◽  
Vol 8 (3) ◽  
pp. 609-619 ◽  
Author(s):  
Dennis Kobelt ◽  
Jutta Aumann ◽  
Manuel Schmidt ◽  
Burghardt Wittig ◽  
Iduna Fichtner ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Preclinical Study ◽  
Tnf Alpha ◽  
Nonviral Gene Therapy ◽  
Dna Vector

Development of a stem cell gene therapy for Sanfilippo syndrome type B

2017 ◽  
Vol 120 (1-2) ◽  
pp. S37 ◽  
Author(s):  
Don L Clarke ◽  
Valentina Sanguez ◽  
Shih Kan ◽  
Steven Lee ◽  
Michelina Iacovino ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Syndrome Type ◽  
Type B ◽  
Sanfilippo Syndrome ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy

Adenovirus-mediated gene transfer in canine eyes: a preclinical study for gene therapy of human uveal melanoma

2001 ◽  
Vol 3 (3) ◽  
pp. 228-239 ◽  
Author(s):  
Mariam Andrawiss ◽  
Anne Maron ◽  
William Beltran ◽  
Paule Opolon ◽  
Elizabeth Connault ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Gene Transfer ◽  
Uveal Melanoma ◽  
Preclinical Study
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