Intracisternal enzyme replacement therapy in lysosomal storage diseases: dispersal pathways, regional enzyme concentrations and the effect of posttreatment posture

2013 ◽  
Vol 39 (6) ◽  
pp. 681-692 ◽  
Author(s):  
R. D. Jolly ◽  
N. R. Marshall ◽  
J. Marshall ◽  
A. Hartman ◽  
K. M. Hemsley ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Lysosomal Storage Diseases ◽  
Lysosomal Storage ◽  
Storage Diseases ◽  
Enzyme Replacement

Management of hypersensitivity reactions to enzyme replacement therapy in children with lysosomal storage diseases

2020 ◽  
Vol 125 (4) ◽  
pp. 460-467
Author(s):  
Irem Turgay Yagmur ◽  
Ozlem Unal Uzun ◽  
Aynur Kucukcongar Yavas ◽  
Ilknur Kulhas Celik ◽  
Muge Toyran ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Lysosomal Storage Diseases ◽  
Hypersensitivity Reactions ◽  
Lysosomal Storage ◽  
Storage Diseases ◽  
Enzyme Replacement

Next-generation antibody-guided enzyme replacement therapy for lysosomal storage diseases

2019 ◽  
Author(s):  
Andrew Baik ◽  
Nina Aaron ◽  
Matthew Birnbaum ◽  
Philip Calafati ◽  
Christopher Schoenherr ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Lysosomal Storage Diseases ◽  
Next Generation ◽  
Lysosomal Storage ◽  
Storage Diseases ◽  
Enzyme Replacement
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