scholarly journals Musings on genome medicine: enzyme-replacement therapy of the lysosomal storage diseases

10.1186/gm114 ◽  
2009 ◽  
Vol 1 (12) ◽  
pp. 114 ◽  
Author(s):  
David G Nathan ◽  
Stuart H Orkin
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Lysosomal Storage Diseases ◽  
Lysosomal Storage ◽  
Storage Diseases ◽  
Enzyme Replacement ◽  
Genome Medicine

Management of hypersensitivity reactions to enzyme replacement therapy in children with lysosomal storage diseases

2020 ◽  
Vol 125 (4) ◽  
pp. 460-467
Author(s):  
Irem Turgay Yagmur ◽  
Ozlem Unal Uzun ◽  
Aynur Kucukcongar Yavas ◽  
Ilknur Kulhas Celik ◽  
Muge Toyran ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Lysosomal Storage Diseases ◽  
Hypersensitivity Reactions ◽  
Lysosomal Storage ◽  
Storage Diseases ◽  
Enzyme Replacement

Next-generation antibody-guided enzyme replacement therapy for lysosomal storage diseases

2019 ◽  
Author(s):  
Andrew Baik ◽  
Nina Aaron ◽  
Matthew Birnbaum ◽  
Philip Calafati ◽  
Christopher Schoenherr ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Lysosomal Storage Diseases ◽  
Next Generation ◽  
Lysosomal Storage ◽  
Storage Diseases ◽  
Enzyme Replacement
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